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Found 362 clinical trials
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  • 27 Feb, 2024
  • 1 location
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  • 05 Feb, 2025
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  • 10 Nov, 2025
  • 2 locations
Test Study For UPENN CRMS Int  

Test Study For UPENN CRMS Int

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  • 27 Feb, 2024
  • 1 location
Fitusiran Prophylaxis in Male Pediatric Subjects Aged 1 to Less Than 12 Years With Hemophilia A or B

Primary Objective: To confirm appropriate dose levels of fitusiran when administered to male pediatric participants (ages 1 to <12 years of age) with severe hemophilia A or B Secondary Objective: To characterize the safety and tolerability To characterize the pharmacokinetics (PK)

fitusiran
haemophilia a
hemophilia
bethesda assay
severe haemophilia a
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  • 04 Dec, 2020
  • 11 locations