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Found 17 clinical trials
Trial without overall contact

without overall contact 

  • 0 views
  • 08 Dec, 2023
  • 1 location
Trial site user Not added

Trial  site user Not added 

  • 0 views
  • 18 Dec, 2023
  • 1 location
over all contact only  

over all contact only 

  • 0 views
  • 18 Dec, 2023
  • 2 locations
Trial for branching logic  

Trial for branching logic

  • 0 views
  • 15 Dec, 2023
  • 1 location
test prescreener  

test prescreener

  • 0 views
  • 19 Dec, 2023
  • 1 location
A Long Term Follow-Up Study of Fabry Disease Subjects Treated With FLT190

This clinical study aims to investigate the long-term safety and durability of GLA in patients who have been dosed with a new gene therapy product (FLT190) in earlier clinical studies.

breakdown
glycosphingolipids
deficiency
fabry's disease
gene therapy
  • 0 views
  • 16 Feb, 2024
  • 1 location
An Open-Label Study to Investigate the Safety of Single Ascending Doses in Children and Adolescents With Dravet Syndrome

Stoke Therapeutics is evaluating the safety and tolerability of single ascending doses of STK-001 in patients with Dravet syndrome. Change in seizure frequency and quality of life will be measured as secondary endpoints in this open-label study.

scn1a gene
ketogenic diet
seizure
epilepsy
dravet syndrome
  • 0 views
  • 05 Aug, 2020