Phenylketonuria Clinical Trials
A listing of Phenylketonuria medical research trials actively recruiting patient volunteers. Search for closest city to find more detailed information on a research study in your area.
Found 268 clinical trials
AAV Gene Therapy Study for Subjects With PKU
This is a Phase 1/2, open-label, dose escalation study to evaluate the safety, efficacy and tolerability of BMN 307 in adult PKU subjects with PAH deficiency. Participants will receive a single administration of BMN 307 and will be followed for safety and efficacy.
- 0 views
- 16 Feb, 2024
- 1 location
Heeba Test Trial
If PKU is not adequately treated, Phe can increase to harmful levels inthe body, causing injury to the brain and the nerves in your body.
- 0 views
- 24 Feb, 2025
- 3 locations
Sujana-A Phase 1/Phase 2 open-label study to evaluate the safety, tolerability, and efficacy of a single intravenous administration of an investigational medication in adult participants with phenylketonuria (PKU)
If PKU is not adequately treated, Phe can increase to harmful levels inthe body, causing injury to the brain and the nerves in your body.
- 0 views
- 13 Nov, 2023
- 1 location
